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周日报道,Crystals强调了PATHFNDS-1和PATHFNDS-2扩展的中期数据,证实了PALSONY治疗肢体肥大症的长期有效性和耐受性

2025-07-14 14:44

  • Data show that PALSONIFY was well tolerated and IGF-1 levels remained stably controlled during long-term open label extensions of PATHFNDR-1 and PATHFNDR-2 studies
  • Additional PALSONIFY presentations demonstrate reductions in patient-reported symptom burden, including both symptom severity and rates of symptom flares

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